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For families

Trial Matching

Answer clinical questions only, then see Duchenne trials that may be worth discussing with your neuromuscular care team.

What is a clinical trial?

Clinical trials are research studies that evaluate potential treatments or interventions. Participation is a personal decision for each family. Consider factors like travel, visit burden, eligibility, your goals, and discussions with your care team.

Educational Use Only

This tool is a starting point for learning. It does not determine eligibility or suitability for a clinical trial and does not provide medical advice. Trial information and eligibility criteria may change. Only the study team can confirm eligibility, and decisions about participation should be made with the individual’s qualified healthcare team.

Note: These clinical questions help rank public trial listings by possible fit. Leave anything blank if you are unsure.

1. Location & Practical Fit

Country

Primary language

Caregiver availability for visits

Travel comfort

Travel / accessibility needs

2. Diagnosis & Genetics

Patient age

Diagnosis status

Mutation / exon information

Genetic report available?

AAV antibody status

Prior gene therapy exposure

Currently enrolled in another interventional study

3. Ambulation & Functional Status

Disease stage

Uses wheelchair?

Most recent 6-minute walk test distance (meters)

6MWT date

NSAA, if known

Recent fall frequency

Can rise from floor? (Gowers)

Upper limb function concern?

4. Steroid Use & Treatment History

Current steroid use

Steroid type

Prior exon-skipping therapy?

Recent medication changes?

Current medications / supplements

5. Cardiac, Pulmonary & Safety Concerns

Most recent LVEF / cardiac status

Cardiac testing within the last 12 months?

Most recent FVC / pulmonary status

Recent major illness, surgery or hospitalization?

Liver concerns / elevated liver enzymes

Immune suppression / infection concerns?

6. Family Priorities & Trial Practical Fit

Main goal right now?

Comfort with placebo-controlled study?

Visit frequency tolerance

Before viewing trial information

I confirm that I am authorized to submit this information. I am either the individual to whom the information relates, the parent or legal guardian of that individual, or another person authorized to provide the information on their behalf.
I understand that the information I enter is used only to generate these one-time educational results. My questionnaire answers are not saved to a DMD Pathways account, patient record, database, browser storage, or ongoing matching profile and are cleared when I leave, refresh, or restart the matching process.
I understand that these results are educational starting points only and do not confirm eligibility or suitability for a clinical trial.
I understand that only the study team can confirm trial eligibility. Trial criteria may change, and decisions about participation should be made with the individual's qualified healthcare team.

Read how DMD Pathways uses information from matching tools